Depression and anxiety are common in children and indicate a problem with mood or anxiety processing. Depression and anxiety disorders can develop in children at any age, from preschool through adolescence. A combination of life experiences, inherited genes, and other factors influence who develops anxiety or depression and when. Depression and anxiety can cause difficulties
We are very pleased to announce our collaboration with Cittadinanzattiva APS, through its branch, Active Citizenship Network (ACN). Cittadinanzattiva APS is an Italian civic organization, founded in 1978, which promotes citizens' activism for the protection of rights, the care of common goods, and the support for people in conditions of weakness. In 2001, the Active
There are still many health conditions which only affect the paediatric population, this would be the case for 80% of rare diseases that lack approved therapeutic options. Clinical trials are essential for the development of new medicines. In the last years, in Europe the number of clinical trials for the paediatric population has increased. At
The Spanish Data Protection Authority published, on last February, the "Code of Conduct on the processing of personal data in the field of clinical trials and other clinical research as well as pharmacovigilance" (CoC). The CoC regulates how data protection rules impact the development of clinical trials and compliance with pharmacovigilance obligations. Regarding clinical trials,
The European post-authorisation study (EU PAS) register is a repository launched in 2010 by the European Medicines Agency. Multi-database studies (MDS) leveraging secondary data have become an important strategy to conduct post-authorization studies (PAS) in recent years. The “Overview of the European post-authorisation study registerpost-authorization studies performed in Europe fromSeptember 2010 to December 2018”, provides
Last February 28th we celebrated Rare Disease Day and Kids Bari, the first Young Persons Advisory Group (YPAG) in Italy, joined the #shareyourcolours campaign by making an amazing video showing their Special Colours. “These Kids and Teens are not defined by their disease, they are not numbers... they are amazing and stunning teens in
As part of the training activities proposed by EJP RD, an online training course on “Training on strategies to foster solutions of undiagnosed rare disease cases” is being organised by Istituto Superiore di Sanità (ISS) in close collaboration with EJP RD partners. The online event will take place over three days from on April 11th – 13th. Through the presentation of sample use cases that
The Therapies Scientific Committee (TSC) of the International Rare Diseases Research Consortium (IRDiRC) is establishing a Task Force to characterize specific commonalities amongst a large group of “disregarded” rare diseases, with the potential secondary aims to identify removable roadblocks that may foster future research and development. The TSC is specifically looking for members to populate the Task Force with the below expertise in one
IRDiRC's Therapies Scientific Committee (TSC) is establishing a Task Force on Drug Repurposing Guidebook aimed at helping developers identify specific tools and practices of relevance for repurposing projects, by focusing on repurposing approaches, following the same successful methodology used for the Orphan Drug Development Guidebook. Interested candidates can submit their application (CV, biosketch and letter of motivation, one paragraph each) to the Scientific Secretariat.
The International Rare Diseases Research Consortium (IRDiRC) is proud to announce the publication of a commentary on 10 years of progress and challenges of IRDiRC in the prestigious journal Nature Reviews Drug Discovery. The article summarizes IRDiRC’s vision and goals and highlights its achievements and prospects after its first decade (2011–2021). The commentary has been authored by Lucia Monaco (Consortium Assembly
